
CRISPR Therapeutics and Vertex Announce FDA Fast Track Designation for CTX001 for the Treatment of Sickle Cell Disease
CRISPR Therapeutics and Vertex Pharmaceuticals Incorporated today announced that the U.S. Food and Drug Administration (FDA) has granted Fast Track Designation...
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Happy Holidays from SCDAA!
The Board of Directors and the staff of the Sickle Cell Disease Association of America, Inc. wish you and your families a safe...
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NBC News Covers the Signing of the Sickle Cell Treatment Act of 2018!
NBC News reporter Chandelis R. Duster wrote an article covering the signing of the Sickle Cell Treatment Act of 2018! Below...
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The President Signs the Sickle Cell Treatment Act of 2018!
Advocacy Efforts Create Legislative Victory! On December 18, 2018, S.2465 – The Sickle Cell Disease and Other Heritable Blood Disorders Research,...
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Read a New Abstract on Camps for Children With Sickle Cell!
Written by Dr. Lewis Hsu, the SCDAA’s Vice Chief Medical Officer, the abstract below is included in a new article published...
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Cincinnati Children’s Hospital Announces 2019 Hemoglobinopathy Counselor Training Course!
For over 10 years, Cincinnati Children’s Hospital Medical Center has offered a comprehensive hemoglobinopathy counselor training course to educate and train...
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Join Us for a Conversation about Sickle Cell!
Mark Your Calendars! We are excited to be partnering with GW School of Medical & Health Sciences, the National Heart, Lung...
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Congress Has Passed the Sickle Cell Treatment Act!
Congress Passed the Sickle Cell Treatment Act of 2018! A Wonderful Victory for the Sickle Cell Community On December 10, 2018, S.2465...
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PRESS RELEASE – GBT Announces the FDA Agrees to Submit a New Drug Application for the Approval of Voxelotor
GBT Announces U.S. FDA Agrees with its Proposal Relating to Accelerated Approval Pathway for Voxelotor for the Treatment of Sickle Cell...
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Rare Disease Week 2019 Preparations are Underway!
Greetings Everyone! It’s that time of year again – Rare Disease Week 2019 preparations are underway! This page contains hyperlinks with important...
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