ASH and FDA Unveil New Recommendations to Guide Clinical Development of Sickle Cell Disease Therapies
Joint FDA/ASH Led Initiative Highlights Importance of Using Patient Reported Outcomes and Biomarkers in Clinical Trials to Advance SCD Therapies (WASHINGTON,... Continue Reading
GBT’s Oxbryta™ (voxelotor) tablets is approved for the treatment of sickle cell disease
Oxbryta™ (voxelotor) tablets Now Approved On behalf of GBT, we are happy to share that Oxbryta (pronounced ox-brye-ta) is now approved... Continue Reading
New Hope for a Sickle Cell Cure
How gene therapy is helping children with this devastating disease. By Joy Harrington, Writer When Mr. and Mrs. Jones married and left... Continue Reading
FDA Approves Global Blood Therapeutics Sickle Cell Disease Drug
(Reuters) – The U.S. Food and Drug Administration said on Monday it approved a drug from Global Blood Therapeutics Inc to... Continue Reading
CRISPR Therapeutics and Vertex Announce Positive Safety and Efficacy Data
Nov 19, 2019 CRISPR Therapeutics and Vertex Announce Positive Safety and Efficacy Data From First Two Patients Treated With Investigational CRISPR/Cas9... Continue Reading
US approves new drug to manage sickle cell disease
By LINDA A. JOHNSON | November 15, 2019 | APNews.com U.S. regulators on Friday approved a new medicine that can help... Continue Reading